Doctors in London have become the first in the world to cure blindness in children born with a rare genetic condition using a pioneering gene therapy.

The children had leber congenital amaurosis (LCA), a severe form of retinal dystrophy that causes vision loss due to a defect in the AIPL1 gene.

After treatment, four children can now see shapes, find toys, recognise their parents’ faces, and in some cases, even read and write.

#science #medicine #GeneTherapy

https://www.theguardian.com/society/2025/feb/20/doctors-in-london-cure-blindness-in-children-with-rare-condition